All muscular dystrophies cause muscle weakness, but life expectancy can vary dramatically between types of muscular dystrophy.
Dr. Mackey’s project, “ Regenerating healthy human skeletal muscle at single nucleus resolution ,” will create the most detailed molecular map to date of how healthy human muscle repairs itself. The ...
Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
Sarepta’s blockbuster gene therapy has come under scrutiny following a string of patient deaths.
Disability advocate TaLisha Gryzb is a mother of four living with muscular dystrophy who educates viewers about her ...
Muscular dystrophies are a group of more than 30 genetic disorders characterized by progressive muscle weakness and wasting. These disorders are typically associated with defects in muscle ...
Skeletal muscle is a dynamic and highly adaptable tissue responsible for voluntary movement, posture and metabolic regulation. Its unique architecture, involving myofibres, satellite cells and a ...
By Mariam Sunny Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for Duchenne muscular dystrophy slowed disease ...
In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...
Dyne Therapeutics leverages its FORCE platform to target genetically driven muscle diseases. Read why I am bullish about DYN ...
"Muscular dystrophy can take many things from me, but it will not take away my happiness, nor will it take away my faith." ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced that on ...